Business Profile

Description: Graphite Bio is a clinical-stage next-generation gene editing company focused on the development of first-in-class therapies for patients suffering from life-threatening genetic diseases. The company’s platform harnesses the natural cellular process of homology directed repair (HDR) and targeted DNA integration to precisely repair genetic defects at their source. Graphite Bio is leveraging its differentiated platform to advance a portfolio of transformative genetic treatments with potential for saving and dramatically improving patients’ lives